Page 161 - MemoriaER-Eng

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We have performed transcriptomic and proteomic studies (in collaboration with
Highlights
the group of CIBERER U732) of various cellular models of frataxin deficiency that

have allowed us to identify some candidates that could serve as biomarkers and
therapeutic targets for Friedreich’s ataxia.

We have initiated two projects aimed at exploring novel approaches for the the-

rapy of Friedreich ataxia, one focused on the development of gene therapy and
another addressing the use of agonists of neurotrophic factor receptors.

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